FDA Approves First Gene Therapy for Sanfilippo Syndrome Type A
Endocrine Balance

FDA Approves First Gene Therapy for Sanfilippo Syndrome Type A

By emily johnson · 302 Views · September 18, 2026

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Three biotech firms eye Nasdaq listings

Three biotech firms—including ADARx Pharma—are preparing Nasdaq listings, with ADARx targeting a $1.74 billion valuation for its hereditary angioedema therapy.

Samoyed 93 Views September 22, 2026
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Biotech and Digital Health Firms Expand Boards

Board appointments are reshaping biotech and digital health firms as August brings seasoned executives and scientific leaders onto boards to drive growth.

Samoyed 200 Views September 21, 2026
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UK drug firms pull out of NICE reviews at record

UK drug firms are pulling out of NICE reviews at record levels in 2026, raising questions about industry shifts or systemic issues in the appraisal process.

Samoyed 223 Views September 19, 2026
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Breast cancer drug Etcamah fails first-line trial test

AstraZeneca’s breast cancer drug Etcamah failed its first-line trial, SERENA-4, raising doubts about its potential as a frontline treatment for HR-positive pati

emily johnson 259 Views September 15, 2026
Endocrine Balance

Biotechs lead fight against cancer

Biotechs lead the fight against cancer with next-generation treatments and clinical trials.

emily johnson 281 Views September 11, 2026